JCR Pharmaceuticals Co., Ltd.

JCR Pharmaceuticals is an R&D-driven pharmaceutical company specializing in rare diseases and biopharmaceuticals. Its defining combination is “a focus on rare diseases + three biopharmaceutical modalities + J-Brain Cargo blood-brain barrier technology.” It develops biopharmaceuticals for rare diseases with small patient populations and no established treatments, including lysosomal storage disorders; its three pillars are recombinant proteins, regenerative medicine, and gene therapy. It also has proprietary J-Brain Cargo technology for crossing the blood-brain barrier. In short, it is a specialty pharmaceutical company applying advanced biopharmaceutical science to rare diseases, headquartered in Ashiya, Hyogo Prefecture.